{"product_id":"cedars-sinai-15th-annual-lysosomal-storage-disease-symposium-2025","title":"Cedars Sinai 15th Annual Lysosomal Storage Disease Symposium 2025","description":"\u003cdiv class=\"columns small-12 medium-12 large-12 sidebar-full\"\u003e\r\n\u003cdiv id=\"MainContent_MainContent_ucLearningActivityCatalog_Details___learningActivityCatalog_TopAndSectionDetails_ucLearningActivityInformation_TopAndSectionDetails_rptLearningActivityInformation_pnllearningActivityInformation_0\" class=\"pnllearningActivityInformationClass\"\u003e\r\n\u003cdiv id=\"MainContent_MainContent_ucLearningActivityCatalog_Details___learningActivityCatalog_TopAndSectionDetails_ucLearningActivityInformation_TopAndSectionDetails_rptLearningActivityInformation_pnlLearningActivityInformationDescription_0\" class=\"pnlLearningActivityInformationDescriptionClass\"\u003e\u003cnav id=\"MainContent_MainContent_ucLearningActivityCatalog_Details___learningActivityCatalog_TopAndSectionDetails_ucLearningActivityInformation_TopAndSectionDetails_rptLearningActivityInformation_navLearningActivityInformation_0\" class=\"navbar nav-gradient factor360CustomStackNavBar\" aria-label=\"open\/close information #1\"\u003e\r\n\u003cdiv id=\"MainContent_MainContent_ucLearningActivityCatalog_Details___learningActivityCatalog_TopAndSectionDetails_ucLearningActivityInformation_TopAndSectionDetails_rptLearningActivityInformation_pnlLearningActivityInformationHeader_0\" class=\"navbar-brand factor360CustomNavBarHeader factor360PageHeaderFlexboxWrapper noBottom\"\u003e\r\n\u003cdiv class=\"woocommerce-tabs wc-tabs-wrapper container tabbed-content\"\u003e\r\n\u003cdiv class=\"tab-panels\"\u003e\r\n\u003cdiv id=\"tab-description\" class=\"woocommerce-Tabs-panel woocommerce-Tabs-panel--description panel entry-content active\" role=\"tabpanel\" aria-labelledby=\"tab-title-description\"\u003e\r\n\u003cdiv id=\"MainContent_MainContent_ucLearningActivityCatalog_Details___learningActivityCatalog_TopAndSectionDetails_ucLearningActivityInformation_TopAndSectionDetails_rptLearningActivityInformation_pnllearningActivityInformation_0\" class=\"pnllearningActivityInformationClass\"\u003e\r\n\u003ch1 class=\"product_title entry-title\"\u003eCedars Sinai 15th Annual Lysosomal Storage Disease Symposium 2025\u003c\/h1\u003e\r\n\u003cstrong\u003e+ Include: 1 videos + 7 pdfs, size: 767 MB\u003c\/strong\u003e\r\n\r\n\u003cstrong\u003e+ Target Audience: physicians, geneticists, neurologists, pediatricians\u003c\/strong\u003e\r\n\r\n\u003cstrong\u003e+ Information:\u003c\/strong\u003e\r\n\u003cdiv class=\"activitysectionbold\"\u003e\r\n\r\nDate \u0026amp; Location: Friday, November 21, 2025, 9:30 AM – 4:05 PM PT, Cedars-Sinai Harvey Morse Conference Center, Los Angeles, CA\r\n\r\n\u003c\/div\u003e\r\n\u003cdiv class=\"activitysectionbold\"\u003eTarget Audience\u003c\/div\u003e\r\n\u003cdiv\u003e\n\u003cem\u003eSpecialties\u003c\/em\u003e – ALL\u003c\/div\u003e\r\n\u003cdiv\u003e\n\u003cem\u003eProfessions\u003c\/em\u003e – Dietitian (Registered Dietitian), Genetic Counselor, Licensed Social Worker, Nurse, Nurse (Advanced Practice NP CRNA CNM CNS), Occupational Therapist, Pharmacist, Physical Therapist, Physician, Physician Assistant, Researcher (non-physician), Researcher (physician)\u003c\/div\u003e\r\n\u003cdiv\u003e\u003c\/div\u003e\r\n\u003cdiv class=\"activitysectionbold\"\u003eOverview\u003c\/div\u003e\r\nThis continuing medical education conference provides a comprehensive update on lysosomal storage disorders (LSDs) for multidisciplinary healthcare teams. LSDs are genetic conditions caused by deficiencies in lysosomal components, primarily enzymes, which lead to lysosomal dysfunction and have widespread effects on peripheral organs and the central nervous system. Participants will explore the latest advances in the identification and diagnosis of LSDs, as well as current understanding of their pathophysiology. The course will also cover updates on management strategies and treatment options, emphasizing the translation of scientific breakthroughs into clinical practice. Expert faculty will present various clinical cases for discussion, along with research updates and case reports that highlight recent developments in the field. This conference aims to enhance the ability of healthcare professionals to provide optimal care for patients with these rare but debilitating disorders, equipping attendees with up-to-date knowledge to improve early diagnosis, implement appropriate management plans, and incorporate emerging therapies into their clinical practice.\r\n\u003cdiv class=\"activitysectionbold\"\u003eObjectives\u003c\/div\u003e\r\n\u003col\u003e\r\n \t\u003cli\u003eApply updated knowledge of lysosomal storage disorders to improve diagnostic accuracy, develop prognoses, contribute to research, and enhance patient care\u003c\/li\u003e\r\n \t\u003cli\u003eIdentify the association between Gaucher disease and cancer\u003c\/li\u003e\r\n \t\u003cli\u003eDescribe the benefits, risks and limitations of newborn screening for lysosomal storage disorders in California\u003c\/li\u003e\r\n \t\u003cli\u003eAnalyze and integrate knowledge of Lysosomal Storage Disorders (LSDs) to collaborate effectively within interprofessional teams, facilitating improved patient care outcomes.\u003c\/li\u003e\r\n\u003c\/ol\u003e\r\nThe \u003cem\u003eCedars-Sinai 15th Annual Lysosomal Storage Disease Symposium 2025\u003c\/em\u003e is best for physicians, geneticists, neurologists, pediatricians, and multidisciplinary healthcare providers who manage patients with lysosomal storage disorders (LSDs). It provides updates on diagnosis, treatment, and research advances, making it especially valuable for clinicians working in metabolic medicine, neurology, pediatrics, and rare disease care.\r\n\u003ch3\u003e Who Should Attend\u003c\/h3\u003e\r\n\u003cul\u003e\r\n \t\u003cli\u003ePhysicians \u0026amp; specialists in neurology, pediatrics, internal medicine, and genetics.\u003c\/li\u003e\r\n \t\u003cli\u003eMetabolic disease experts managing LSDs such as Gaucher, Fabry, Pompe, and MPS disorders.\u003c\/li\u003e\r\n \t\u003cli\u003eAdvanced practice providers (NPs, PAs) working in rare disease or neurology clinics.\u003c\/li\u003e\r\n \t\u003cli\u003eResearchers \u0026amp; academic faculty studying lysosomal biology and therapeutic innovations.\u003c\/li\u003e\r\n \t\u003cli\u003eMultidisciplinary teams (nurses, pharmacists, therapists) involved in patient care.\u003c\/li\u003e\r\n\u003c\/ul\u003e\r\n\u003ch3\u003e What You’ll Learn\u003c\/h3\u003e\r\n\u003cul\u003e\r\n \t\u003cli\u003eLatest advances in LSDs: updates on pathophysiology, genetics, and clinical manifestations.\u003c\/li\u003e\r\n \t\u003cli\u003eTherapeutic innovations: enzyme replacement therapy, substrate reduction, gene therapy.\u003c\/li\u003e\r\n \t\u003cli\u003eMultisystem involvement: neurological, cardiac, skeletal, and visceral complications.\u003c\/li\u003e\r\n \t\u003cli\u003eCase‑based learning: practical approaches to diagnosis and long‑term management.\u003c\/li\u003e\r\n \t\u003cli\u003eFuture directions: clinical trials, biomarkers, and personalized medicine strategies.\u003c\/li\u003e\r\n\u003c\/ul\u003e\r\n \r\n\r\n\u003cstrong\u003e+ Topics:\u003c\/strong\u003e\r\n\u003cul\u003e\r\n \t\u003cli\u003eRecording.mp4\u003c\/li\u003e\r\n \t\u003cli\u003eWelcome and Introduction.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eBreakthroughs in Treatment for LSDs.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eCancer in Gaucher Disease.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eClinical Case 1.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eClinical Case 2.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eGaucher Disease – Clinical Updates.pdf\u003c\/li\u003e\r\n \t\u003cli\u003eGaucher Disease – Research Updates.pdf\u003c\/li\u003e\r\n\u003c\/ul\u003e\r\n\u003c\/div\u003e\r\n\u003c\/div\u003e\r\n\u003c\/div\u003e\r\n\u003c\/div\u003e\r\n\u003c\/div\u003e\r\n\u003c\/nav\u003e\u003c\/div\u003e\r\n\u003c\/div\u003e\r\n\u003c\/div\u003e","brand":"meducours","offers":[{"title":"Default Title","offer_id":42954673029218,"sku":"MED-AMB07945","price":10.0,"currency_code":"USD","in_stock":true}],"thumbnail_url":"\/\/cdn.shopify.com\/s\/files\/1\/0662\/9549\/6802\/files\/Cedars-Sinai-15th-Annual-Lysosomal-Storage-Disease-Symposium-2025.jpg?v=1779382173","url":"https:\/\/meducourse.com\/products\/cedars-sinai-15th-annual-lysosomal-storage-disease-symposium-2025","provider":"Meducourse","version":"1.0","type":"link"}