{"product_id":"rna-therapeutics-institute-rna-therapeutics-from-concept-to-clinic-2025","title":"RNA Therapeutics Institute RNA Therapeutics From Concept to Clinic 2025","description":"\u003cdiv class=\"prod-filesize\"\u003e\n\u003cdiv class=\"prod-edition\"\u003e\n\u003ch1 class=\"product_title entry-title\"\u003eRNA Therapeutics Institute RNA Therapeutics From Concept to Clinic 2025\u003c\/h1\u003e\n\u003cstrong\u003e+ Include: 3 videos + 1 pdf, size: 83.51 GB\u003c\/strong\u003e\n\u003cbr\u003e\u003cstrong\u003e+ Target Audience: R\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategy professionals, manufacturing\/operations managers\u003c\/strong\u003e\n\u003cbr\u003e\u003cstrong\u003e+ Information:\u003c\/strong\u003e\n\u003cbr\u003e\u003cp data-end=\"406\" data-start=\"80\"\u003eA translational, bench-to-bedside program covering the full lifecycle of RNA medicines. Faculty connect platform science (siRNA, ASO, mRNA, saRNA, emerging circular RNA) with delivery, CMC, regulatory strategy, and clinical development—so teams can move candidates efficiently and safely toward approval.\u003c\/p\u003e\n\u003cp data-end=\"433\" data-start=\"408\"\u003e\u003cstrong data-end=\"431\" data-start=\"408\"\u003eWhat You Will Learn\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"1353\" data-start=\"434\"\u003e\n\u003cli data-end=\"553\" data-start=\"434\"\u003e\n\u003cp data-end=\"553\" data-start=\"436\"\u003eModality selection \u0026amp; design: choosing siRNA vs. ASO vs. (sa)mRNA vs. circRNA; chemistries, modifications, stability\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"660\" data-start=\"554\"\u003e\n\u003cp data-end=\"660\" data-start=\"556\"\u003eDelivery systems: LNPs, GALNAc conjugates, polymer\/peptide carriers, local vs. systemic administration\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"776\" data-start=\"661\"\u003e\n\u003cp data-end=\"776\" data-start=\"663\"\u003ePreclinical translation: in vitro\/in vivo models, PK\/PD, biodistribution, immunogenicity, off-target assessment\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"885\" data-start=\"777\"\u003e\n\u003cp data-end=\"885\" data-start=\"779\"\u003eCMC fundamentals: process development, analytics, release\/stability testing, scale-up, and tech transfer\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"999\" data-start=\"886\"\u003e\n\u003cp data-end=\"999\" data-start=\"888\"\u003eClinical development: FIH design, dose selection, biomarkers, patient selection, endpoints, safety monitoring\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1115\" data-start=\"1000\"\u003e\n\u003cp data-end=\"1115\" data-start=\"1002\"\u003eRegulatory \u0026amp; quality: IND\/IMPD strategy, comparability, potency assays, pharm-tox expectations, risk management\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1232\" data-start=\"1116\"\u003e\n\u003cp data-end=\"1232\" data-start=\"1118\"\u003eManufacturing operations: raw materials, supply chain, single-use workflows, contamination control, cost drivers\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1353\" data-start=\"1233\"\u003e\n\u003cp data-end=\"1353\" data-start=\"1235\"\u003eData \u0026amp; tools: sequence optimization, secondary structure prediction, bioinformatics\/AI for target\/off-target profiling\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp data-end=\"1374\" data-start=\"1355\"\u003e\u003cstrong data-end=\"1372\" data-start=\"1355\"\u003eEvent Details\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"1650\" data-start=\"1375\"\u003e\n\u003cli data-end=\"1448\" data-start=\"1375\"\u003e\n\u003cp data-end=\"1448\" data-start=\"1377\"\u003eFormat: Case-based lectures, panel Q\u0026amp;A, and short technical workshops\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1556\" data-start=\"1449\"\u003e\n\u003cp data-end=\"1556\" data-start=\"1451\"\u003eStructure: Concept\/design → delivery\/PKPD → CMC\/manufacturing → clinical\/regulatory → commercialization\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1650\" data-start=\"1557\"\u003e\n\u003cp data-end=\"1650\" data-start=\"1559\"\u003eTakeaways: Checklists, study-design templates, and CMC\/quality worksheets for immediate use\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp data-end=\"1878\" data-start=\"1652\"\u003e\u003cstrong data-end=\"1673\" data-start=\"1652\"\u003eWho Should Attend\u003c\/strong\u003e\u003cbr\u003eR\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategic affairs, manufacturing\/operations managers, platform founders, investors, and trainees entering the RNA space.\u003c\/p\u003e\n\u003cp data-end=\"1896\" data-start=\"1880\"\u003e\u003cstrong data-end=\"1894\" data-start=\"1880\"\u003eWhy Attend\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"2135\" data-start=\"1897\"\u003e\n\u003cli data-end=\"1972\" data-start=\"1897\"\u003e\n\u003cp data-end=\"1972\" data-start=\"1899\"\u003eReplace trial-and-error with validated design and development playbooks\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"2052\" data-start=\"1973\"\u003e\n\u003cp data-end=\"2052\" data-start=\"1975\"\u003eAnticipate regulatory and manufacturing pitfalls early to de-risk timelines\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"2135\" data-start=\"2053\"\u003e\n\u003cp data-end=\"2135\" data-start=\"2055\"\u003eAlign discovery, CMC, and clinical groups around practical, decision-ready tools\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cbr\u003e \u003cbr\u003e\u003cbr\u003e\u003cstrong\u003e+ Topics:\u003c\/strong\u003e\u003cbr\u003e\u003cbr\u003e*Note: these are continuous video recordings during the conference, they include individual lectures mentioned in the Detail section below\u003cbr\u003e\u003cul\u003e\n\u003cli\u003eJune 25, 2025.mp4\u003c\/li\u003e\n\u003cli\u003eJune 26, 2025.mp4\u003c\/li\u003e\n\u003cli\u003eJune 27, 2025.mp4\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003c\/div\u003e\n\u003c\/div\u003e","brand":"meducours","offers":[{"title":"Default Title","offer_id":42954525016162,"sku":"MED-AMB05295","price":40.0,"currency_code":"USD","in_stock":true}],"thumbnail_url":"\/\/cdn.shopify.com\/s\/files\/1\/0662\/9549\/6802\/files\/RNA-Therapeutics-Institute-RNA-Therapeutics-From-Concept-to-Clinic-2025.jpg?v=1779378872","url":"https:\/\/meducourse.com\/products\/rna-therapeutics-institute-rna-therapeutics-from-concept-to-clinic-2025","provider":"Meducourse","version":"1.0","type":"link"}