{"product_id":"rna-therapeutics-institute-rna","title":"RNA Therapeutics Institute RNA Therapeutics From Concept to Clinic 2024","description":"\u003ch3\u003eRNA Therapeutics Institute RNA Therapeutics From Concept to Clinic 2024\u003c\/h3\u003e\n\u003cstrong\u003e+ Target Audience: R\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategy professionals,\u003c\/strong\u003e\n\u003cbr\u003e\u003cstrong\u003e manufacturing\/operations managers\u003c\/strong\u003e\n\u003cbr\u003e\u003cstrong\u003e+ Information:\u003c\/strong\u003e\n\u003cbr\u003e\u003cp data-end=\"384\" data-start=\"80\"\u003eA translational, bench-to-bedside program covering the full lifecycle of RNA medicines. Faculty connect platform science (siRNA, ASO, mRNA, saRNA) with delivery, CMC, regulatory strategy, and clinical development to help teams move candidates efficiently and safely toward approval.\u003c\/p\u003e\n\u003cp data-end=\"411\" data-start=\"386\"\u003e\u003cstrong data-end=\"409\" data-start=\"386\"\u003eWhat You Will Learn\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"1426\" data-start=\"412\"\u003e\n\u003cli data-end=\"515\" data-start=\"412\"\u003e\n\u003cp data-end=\"515\" data-start=\"414\"\u003eModality selection and design: siRNA vs. ASO vs. (sa)mRNA—chemistries, modifications, and stability\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"615\" data-start=\"516\"\u003e\n\u003cp data-end=\"615\" data-start=\"518\"\u003eDelivery systems: LNPs, GALNAc conjugates, polymers\/peptides, local vs. systemic administration\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"728\" data-start=\"616\"\u003e\n\u003cp data-end=\"728\" data-start=\"618\"\u003ePreclinical translation: in vitro\/in vivo models, PK\/PD, biodistribution, immunogenicity and off-target risk\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"836\" data-start=\"729\"\u003e\n\u003cp data-end=\"836\" data-start=\"731\"\u003eCMC fundamentals: process development, analytics, release\/stability testing, scale-up and tech transfer\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"954\" data-start=\"837\"\u003e\n\u003cp data-end=\"954\" data-start=\"839\"\u003eClinical development: FIH design, dose selection, biomarkers, patient selection, endpoints, and safety monitoring\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1074\" data-start=\"955\"\u003e\n\u003cp data-end=\"1074\" data-start=\"957\"\u003eRegulatory \u0026amp; quality: IND\/IMPD packages, comparability, potency assays, pharm tox expectations, and risk management\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1194\" data-start=\"1075\"\u003e\n\u003cp data-end=\"1194\" data-start=\"1077\"\u003eManufacturing operations: raw materials (lipids, nucleotides, enzymes), single-use workflows, contamination control\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1322\" data-start=\"1195\"\u003e\n\u003cp data-end=\"1322\" data-start=\"1197\"\u003eData \u0026amp; tools: sequence optimization, secondary structure prediction, bioinformatics\/AI for target and off-target assessment\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1426\" data-start=\"1323\"\u003e\n\u003cp data-end=\"1426\" data-start=\"1325\"\u003eAccess \u0026amp; value: manufacturing cost drivers, IP strategy, partnerships, and commercialization pathways\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp data-end=\"1447\" data-start=\"1428\"\u003e\u003cstrong data-end=\"1445\" data-start=\"1428\"\u003eEvent Details\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"1723\" data-start=\"1448\"\u003e\n\u003cli data-end=\"1521\" data-start=\"1448\"\u003e\n\u003cp data-end=\"1521\" data-start=\"1450\"\u003eFormat: Case-based lectures, panel Q\u0026amp;A, and short technical workshops\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1629\" data-start=\"1522\"\u003e\n\u003cp data-end=\"1629\" data-start=\"1524\"\u003eStructure: Concept\/design → delivery\/PKPD → CMC\/manufacturing → clinical\/regulatory → commercialization\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"1723\" data-start=\"1630\"\u003e\n\u003cp data-end=\"1723\" data-start=\"1632\"\u003eTakeaways: Checklists, study-design templates, and CMC\/quality worksheets for immediate use\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp data-end=\"1968\" data-start=\"1725\"\u003e\u003cstrong data-end=\"1746\" data-start=\"1725\"\u003eWho Should Attend\u003c\/strong\u003e\u003cbr\u003eR\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategy professionals, manufacturing\/operations managers, platform and biotech founders, investors, and trainees entering the RNA space.\u003c\/p\u003e\n\u003cp data-end=\"1986\" data-start=\"1970\"\u003e\u003cstrong data-end=\"1984\" data-start=\"1970\"\u003eWhy Attend\u003c\/strong\u003e\u003c\/p\u003e\n\u003cul data-end=\"2236\" data-start=\"1987\"\u003e\n\u003cli data-end=\"2062\" data-start=\"1987\"\u003e\n\u003cp data-end=\"2062\" data-start=\"1989\"\u003eReplace trial-and-error with validated design and development playbooks\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"2142\" data-start=\"2063\"\u003e\n\u003cp data-end=\"2142\" data-start=\"2065\"\u003eAnticipate regulatory and manufacturing pitfalls early to de-risk timelines\u003c\/p\u003e\n\u003c\/li\u003e\n\u003cli data-end=\"2236\" data-start=\"2143\"\u003e\n\u003cp data-end=\"2236\" data-start=\"2145\"\u003eBring back practical tools to align discovery, CMC, and clinical teams around the same plan\u003c\/p\u003e\n\u003c\/li\u003e\n\u003c\/ul\u003e\u003cbr\u003e \u003cbr\u003e\u003cbr\u003e\u003cstrong\u003e+ Topics:\u003c\/strong\u003e\u003cbr\u003e\u003cbr\u003e* Detail:\u003cbr\u003e\u003cbr\u003e\u003cimg src=\"https:\/\/cdn.shopify.com\/s\/files\/1\/0720\/8619\/2282\/files\/screenshot-2024-05-24-at-11.46.35am.png?v=1770208101\"\u003e\u003cimg alt=\"Day 3- RNATx Program\" src=\"https:\/\/cdn.shopify.com\/s\/files\/1\/0720\/8619\/2282\/files\/screenshot-2024-05-24-at-11.46.53am.png?v=1770208104\"\u003e","brand":"meducours","offers":[{"title":"Default Title","offer_id":42954502602850,"sku":"MED-AMB04792","price":30.0,"currency_code":"USD","in_stock":true}],"thumbnail_url":"\/\/cdn.shopify.com\/s\/files\/1\/0662\/9549\/6802\/files\/RNA-Therapeutics-Institute-RNA-Therapeutics-From-Concept-to-Clinic-2024-1.webp?v=1779378269","url":"https:\/\/meducourse.com\/products\/rna-therapeutics-institute-rna","provider":"Meducourse","version":"1.0","type":"link"}